Concepedia

Publication | Open Access

A phase 3 randomized study evaluating sialic acid extended-release for GNE myopathy

DOIFull Paper Access

77

Citations

26

References

2019

Year

Hanns Lochmüller, Anthony Béhin, Yoseph Caraco, Heather Lau, Massimiliano Mirabella, Ivailo Tournev, Mark A. Tarnopolsky, Oksana Pogoryelova, C. G. Woods, Alexander C. Lai,
Neurology

Abstract

This study provides Class I evidence that for patients with GNE myopathy, Ace-ER does not improve muscle strength compared to placebo.

References

YearCitations

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