Alban Vignaud

Muscle inactivation of mTOR causes metabolic and dystrophin defects leading to severe myopathy

Valérie Risson, Laetitia Mazelin, Mila Roceri et al. · The Journal of Cell Biology · 2009 · 377 citations · Full text

Medicine, Neurology, Pathology +14

Misregulated alternative splicing of BIN1 is associated with T tubule alterations and muscle weakness in myotonic dystrophy

Charlotte Fugier, Arnaud F. Klein, Caroline Hammer et al. · Nature Medicine · 2011 · 330 citations

Medicine, Genetics, Molecular Biology +11

Antigen-selective modulation of AAV immunogenicity with tolerogenic rapamycin nanoparticles enables successful vector re-administration

Amine Meliani, Florence Boisgérault, Romain Hardet et al. · Nature Communications · 2018 · 254 citations · Full text

Pharmacy, Biotechnology, Immunology +17

Influence of Pre-existing Anti-capsid Neutralizing and Binding Antibodies on AAV Vector Transduction

Zachary Fitzpatrick, Christian Leborgne, Elena Barbon et al. · Molecular Therapy — Methods & Clinical Development · 2018 · 197 citations · Full text

Life Sciences, Immunology, Molecular Biology +13

Gene Therapy Prolongs Survival and Restores Function in Murine and Canine Models of Myotubular Myopathy

Martin K. Childers, Romain Joubert, Karine Poulard et al. · Science Translational Medicine · 2014 · 170 citations · Full text

Medicine, Molecular Genetics, Molecular Medicine +16