Deepak B. Thimiri Govinda Raj

Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B

Amit Nathwani, Ulreke M. Reiss, Edward G. D. Tuddenham et al. · New England Journal of Medicine · 2014 · 1.3K citations · Full text

Medicine, Genetics, Molecular Genetics +17

Long-term Safety and Efficacy Following Systemic Administration of a Self-complementary AAV Vector Encoding Human FIX Pseudotyped With Serotype 5 and 8 Capsid Proteins

Amit C. Nathwani, Cecilia Rosales, Jenny McIntosh et al. · Molecular Therapy · 2011 · 350 citations · Full text

Life Sciences, Molecular Biology, Molecular Genetics +14

Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant

Jenny McIntosh, Peter J. Lenting, Cecilia Rosales et al. · Blood · 2013 · 277 citations

Medicine, Hematology, Pharmacology +14

Switchable CAR-T cells mediate remission in metastatic pancreatic ductal adenocarcinoma

Deepak B. Thimiri Govinda Raj, Ming-Hsin Yang, David T. Rodgers et al. · Gut · 2018 · 149 citations · Full text

Life Sciences, Immunology, Oncology +17

MiR-93 Controls Adiposity via Inhibition of Sirt7 and Tbx3

Michele Cioffi, Mireia Vallespinos-Serrano, Sara Maria David Trabulo et al. · Cell Reports · 2015 · 123 citations · Full text

Life Sciences, Genetics, Molecular Biology +12