Nicole Gusset

Disease impact on general well-being and therapeutic expectations of European Type II and Type III spinal muscular atrophy patients

Françoise Rouault, Vanessa Christie-Brown, Ria Broekgaarden et al. · Neuromuscular Disorders · 2017 · 125 citations

Health Professions, Health Sciences, Behavioral Health +14

Understanding European patient expectations towards current therapeutic development in spinal muscular atrophy

Nicole Gusset, Caroline Stalens, Eva Stumpe et al. · Neuromuscular Disorders · 2021 · 50 citations

Medicine, Pharmacotherapy, Good Clinical Practice +13

Patient and parent oriented tools to assess health-related quality of life, activity of daily living and caregiver burden in SMA. Rome, 13 July 2019

Eugenio Mercuri, Sonia Messina, Jacqueline Montes et al. · Neuromuscular Disorders · 2020 · 26 citations · Full text

Pharmacy, Child Health, Family Assessment +14

A Patient-Centered Evaluation of Meaningful Change on the 32-Item Motor Function Measure in Spinal Muscular Atrophy Using Qualitative and Quantitative Data

Tina Duong, Hannah Staunton, Jessica Braid et al. · Frontiers in Neurology · 2022 · 26 citations · Full text

Medicine, Neurology, Rehabilitation Medicine +16

Understanding the relationship between the 32-item motor function measure and daily activities from an individual with spinal muscular atrophy and their caregivers’ perspective: a two-part study

Tina Duong, Jessica Braid, Hannah Staunton et al. · BMC Neurology · 2021 · 18 citations · Full text

Medicine, Neurology, Rehabilitation Medicine +17