Tina Duong

Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy: a prospective cohort study

Craig M. McDonald, Erik Henricson, Richard T. Abresch et al. · The Lancet · 2017 · 446 citations

Long-term Effects, Duchenne Muscular Dystrophy, Degenerative Disease +4

Revised upper limb module for spinal muscular atrophy: Development of a new module

Elena Mazzone, Anna Mayhew, Jacqueline Montes et al. · Muscle & Nerve · 2016 · 342 citations

Content validity and clinical meaningfulness of the HFMSE in spinal muscular atrophy

Maria Carmela Pera, Giorgia Coratti, Nicola Forcina et al. · BMC Neurology · 2017 · 209 citations · Full text

The cooperative international neuromuscular research group Duchenne natural history study: Glucocorticoid treatment preserves clinically meaningful functional milestones and reduces rate of disease progression as measured by manual muscle testing and other commonly used clinical trial outcome measures

Erik Henricson, Richard T. Abresch, Avital Cnaan et al. · Muscle & Nerve · 2013 · 197 citations

Prednisone/prednisolone and deflazacort regimens in the CINRG Duchenne Natural History Study

Luca Bello, Heather Gordish‐Dressman, Lauren P. Morgenroth et al. · Neurology · 2015 · 197 citations · Full text