Attilio Rovelli

Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy

Alessandra Biffi, Eugenio Montini, Laura Lorioli et al. · Science · 2013 · 1.2K citations · Full text

Life Sciences, Genetics, Hematology +16

Defibrotide for prophylaxis of hepatic veno-occlusive disease in paediatric haemopoietic stem-cell transplantation: an open-label, phase 3, randomised controlled trial

Selim Corbacioglu, Simone Cesaro, Maura Faraci et al. · The Lancet · 2012 · 375 citations

Medicine, Hematology, Pediatrics +12

Long-term outcome of Hurler syndrome patients after hematopoietic cell transplantation: an international multicenter study

Mieke Aldenhoven, Robert Wynn, Paul J. Orchard et al. · Blood · 2015 · 317 citations · Full text

Medicine, Hematology, Stem Cell Transplantation +15

Enzyme replacement therapy and/or hematopoietic stem cell transplantation at diagnosis in patients with mucopolysaccharidosis type I: results of a European consensus procedure

Minke H. de Ru, Jaap Jan Boelens, Anibh M. Das et al. · Orphanet Journal of Rare Diseases · 2011 · 234 citations · Full text

Medicine, Hematology, Pathology +8

Treatment of Graft versus Host Disease with Mesenchymal Stromal Cells: A Phase I Study on 40 Adult and Pediatric Patients

Martino Introna, Giovanna Lucchini, Erica Dander et al. · Biology of Blood and Marrow Transplantation · 2013 · 214 citations · Full text

Medicine, Hematology, Pediatrics +15