Denise A. Carbonaro

T lymphocytes with a normal ADA gene accumulate after transplantation of transduced autologous umbilical cord blood CD34+ cells in ADA-deficient SCID neonates

Donald B. Kohn, Michal S. Hershfield, Denise A. Carbonaro et al. · Nature Medicine · 1998 · 329 citations · Full text

Cell Therapy, Transplantation, Autoimmune Disease +12

A Clinical Trial of Retroviral-Mediated Transfer of arev-Responsive Element Decoy Gene Into CD34+Cells From the Bone Marrow of Human Immunodeficiency Virus-1–Infected Children

Donald B. Kohn, Gerhard Bauer, Chantelle Rice et al. · Blood · 1999 · 257 citations

Gene therapy for adenosine deaminase–deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans

Fabio Candotti, Kit L. Shaw, Linda Muul et al. · Blood · 2012 · 233 citations · Full text

Clonality analysis after retroviral-mediated gene transfer to CD34+ cells from the cord blood of ADA-deficient SCID neonates

Manfred Schmidt, Denise A. Carbonaro, Carsten Speckmann et al. · Nature Medicine · 2003 · 133 citations

Clonality Analysis, Immunology, Hematology +9

Neonatal Gene Therapy of MPS I Mice by Intravenous Injection of a Lentiviral Vector

Hiroshi Kobayashi, Denise A. Carbonaro, Karen Pepper et al. · Molecular Therapy · 2005 · 126 citations · Full text