Paola Tiberi

Intein-mediated protein trans-splicing expands adeno-associated virus transfer capacity in the retina

Patrizia Tornabene, Ivana Trapani, Renato Minopoli et al. · Science Translational Medicine · 2019 · 187 citations · Full text

Life Sciences, Molecular Biology, Ophthalmology +14

Triple Vectors Expand AAV Transfer Capacity in the Retina

Andrea Maddalena, Patrizia Tornabene, Paola Tiberi et al. · Molecular Therapy · 2017 · 124 citations · Full text

Medicine, Molecular Biology, Ophthalmology +9

Light‐responsive microRNA miR‐211 targets Ezrin to modulate lysosomal biogenesis and retinal cell clearance

Federica Naso, Daniela Intartaglia, Danila Falanga et al. · The EMBO Journal · 2020 · 47 citations · Full text

Life Sciences, Cell Biology, Molecular Biology +11

Retinal gene therapy for Stargardt disease with dual AAV intein vectors is both safe and effective in large animal models

Rita Ferla, Eugenio Pugni, Mariangela Lupo et al. · Science Advances · 2025 · 15 citations · Full text

Medicine, Ophthalmology, Vision Science +17

High-Throughput Screening Identifies Kinase Inhibitors That Increase Dual Adeno-Associated Viral Vector Transduction <i>In Vitro</i> and in Mouse Retina

Andrea Maddalena, Fabio Dell’Aquila, Pia Giovannelli et al. · Human Gene Therapy · 2018 · 14 citations · Full text

Life Sciences, Molecular Biology, Ophthalmology +14