Fabio Dell’Aquila

Intein-mediated protein trans-splicing expands adeno-associated virus transfer capacity in the retina

Patrizia Tornabene, Ivana Trapani, Renato Minopoli et al. · Science Translational Medicine · 2019 · 177 citations · Full text

Efficacy, pharmacokinetics, and safety in the mouse and primate retina of dual AAV vectors for Usher syndrome type 1B

Rita Ferla, Fabio Dell’Aquila, Monica Doria et al. · Molecular Therapy — Methods & Clinical Development · 2023 · 24 citations · Full text

Liver‐directed gene therapy for ornithine aminotransferase deficiency

Iolanda Boffa, Elena Polishchuk, Lucia De Stefano et al. · EMBO Molecular Medicine · 2023 · 17 citations · Full text

Safe and effective liver-directed AAV-mediated homology-independent targeted integration in mouse models of inherited diseases

Federica Esposito, Fabio Dell’Aquila, Manuel Rhiel et al. · Cell Reports Medicine · 2024 · 15 citations · Full text

High-Throughput Screening Identifies Kinase Inhibitors That Increase Dual Adeno-Associated Viral Vector Transduction <i>In Vitro</i> and in Mouse Retina

Andrea Maddalena, Fabio Dell’Aquila, Pia Giovannelli et al. · Human Gene Therapy · 2018 · 14 citations · Full text