Arun K. Krishnan

Intravitreal antisense oligonucleotide sepofarsen in Leber congenital amaurosis type 10: a phase 1b/2 trial

Stephen R. Russell, Arlene V. Drack, Artur V. Cideciyan et al. · Nature Medicine · 2022 · 130 citations · Full text

Medicine, Ophthalmology, Pharmacotherapy +13

Durable vision improvement after a single treatment with antisense oligonucleotide sepofarsen: a case report

Artur V. Cideciyan, Samuel G. Jacobson, Allen C. Ho et al. · Nature Medicine · 2021 · 63 citations · Full text

Medicine, Ophthalmology, Vision Science +4

Safety and improved efficacy signals following gene therapy in childhood blindness caused by GUCY2D mutations

Samuel G. Jacobson, Artur V. Cideciyan, Allen C. Ho et al. · iScience · 2021 · 45 citations · Full text

Life Sciences, Genetics, Pediatrics +17

Treatment Potential for Macular Cone Vision in Leber Congenital Amaurosis Due to<i>CEP290</i>or<i>NPHP5</i>Mutations: Predictions From Artificial Intelligence

Alexander Sumaroka, Alexandra V. Garafalo, Evelyn P. Semenov et al. · Investigative Ophthalmology & Visual Science · 2019 · 36 citations · Full text

Medicine, Genetics, Ophthalmology +17

Night vision restored in days after decades of congenital blindness

Samuel G. Jacobson, Artur V. Cideciyan, Allen C. Ho et al. · iScience · 2022 · 36 citations · Full text

Medicine, Neuroscience, Ophthalmology +14