Mariane de Montalembert

CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia

Haydar Frangoul, David Altshuler, Maria Domenica Cappellini et al. · New England Journal of Medicine · 2020 · 1.7K citations · Full text

Gene Therapy in a Patient with Sickle Cell Disease

Jean‐Antoine Ribeil, Salima Hacein‐Bey‐Abina, Emmanuel Payen et al. · New England Journal of Medicine · 2017 · 658 citations · Full text

Immunohematology, Gene Therapies, Busulfan Conditioning +15

Exagamglogene Autotemcel for Severe Sickle Cell Disease

Haydar Frangoul, Franco Locatelli, Akshay Sharma et al. · New England Journal of Medicine · 2024 · 304 citations

Recommendations regarding splenectomy in hereditary hemolytic anemias

Achille Iolascon, Immacolata Andolfo, Wilma Barcellini et al. · Haematologica · 2017 · 206 citations · Full text

Anemia, Immunohematology, Laboratory Hematology +12

Impact of sickle cell disease on patientsʼ daily lives, symptoms reported, and disease management strategies: Results from the international <scp>Sickle Cell World Assessment Survey</scp> (<scp>SWAY</scp>)

Ifeyinwa Osunkwo, Biree Andemariam, Caterina P. Minniti et al. · American Journal of Hematology · 2020 · 168 citations · Full text