Kimberly Zaraspe

Correction of Neurological Disease of Mucopolysaccharidosis IIIB in Adult Mice by rAAV9 Trans-Blood–Brain Barrier Gene Delivery

Haiyan Fu, Julianne DiRosario, Smruti Killedar et al. · Molecular Therapy · 2011 · 195 citations · Full text

Patterns of scAAV Vector Insertion Associated With Oncogenic Events in a Mouse Model for Genotoxicity

Lucia E. Rosas, Jessica Grieves, Kimberly Zaraspe et al. · Molecular Therapy · 2012 · 97 citations · Full text

Functional correction of neurological and somatic disorders at later stages of disease in MPS IIIA mice by systemic scAAV9-hSGSH gene delivery

Haiyan Fu, Marcela P. Cataldi, Tierra Ware et al. · Molecular Therapy — Methods & Clinical Development · 2016 · 58 citations · Full text

Immunology, Functional Correction, Mps Iiia +18

Broad Functional Correction of Molecular Impairments by Systemic Delivery of scAAVrh74-hSGSH Gene Delivery in MPS IIIA Mice

F. Jason Duncan, Bartholomew J. Naughton, Kimberly Zaraspe et al. · Molecular Therapy · 2015 · 25 citations · Full text

Root Cause, Immunology, Gene Delivery +17

A GLP-Compliant Toxicology and Biodistribution Study: Systemic Delivery of an rAAV9 Vector for the Treatment of Mucopolysaccharidosis IIIB

Aaron S. Meadows, F. Jason Duncan, Marybeth Camboni et al. · Human Gene Therapy Clinical Development · 2015 · 21 citations · Full text