Jana Miniarikova

AAV5-miHTT Gene Therapy Demonstrates Broad Distribution and Strong Human Mutant Huntingtin Lowering in a Huntington’s Disease Minipig Model

Melvin M. Evers, Jana Miniarikova, Štefan Juhás et al. · Molecular Therapy · 2018 · 157 citations · Full text

Design, Characterization, and Lead Selection of Therapeutic miRNAs Targeting Huntingtin for Development of Gene Therapy for Huntington's Disease

Jana Miniarikova, Ilaria Zanella, Angelina Huseinovic et al. · Molecular Therapy — Nucleic Acids · 2016 · 131 citations · Full text

AAV5-miHTT gene therapy demonstrates suppression of mutant huntingtin aggregation and neuronal dysfunction in a rat model of Huntington’s disease

Jana Miniarikova, Virginie Zimmer, Raygene Martier et al. · Gene Therapy · 2017 · 100 citations · Full text

Genetics, Rat Model, Mutant Huntingtin Aggregation +18

Preclinical Evaluation of a Lentiviral Vector for Huntingtin Silencing

Karine Cambon, Virginie Zimmer, Sylvain Martineau et al. · Molecular Therapy — Methods & Clinical Development · 2017 · 15 citations · Full text