Myriam Rai

HDAC Inhibitors Correct Frataxin Deficiency in a Friedreich Ataxia Mouse Model

Myriam Rai, Elisabetta Soragni, Kai Jenssen et al. · PLoS ONE · 2008 · 211 citations · Full text

Progression characteristics of the European Friedreich’s Ataxia Consortium for Translational Studies (EFACTS): a 2 year cohort study

Kathrin Reetz, Imis Dogan, R.-D Hilgers et al. · The Lancet Neurology · 2016 · 150 citations

Neurodegenerative Diseases, Neurobiology Of Disease, Progression Characteristics +11

Neurons and cardiomyocytes derived from induced pluripotent stem cells as a model for mitochondrial defects in Friedreich's ataxia

Aurore Hick, Marie Wattenhofer‐Donzé, Satyan Chintawar et al. · Disease Models & Mechanisms · 2012 · 148 citations · Full text

Epigenetic therapy for <scp>F</scp>riedreich ataxia

Elisabetta Soragni, Wenyan Miao, Marco Iudicello et al. · Annals of Neurology · 2014 · 142 citations · Full text

Two New Pimelic Diphenylamide HDAC Inhibitors Induce Sustained Frataxin Upregulation in Cells from Friedreich's Ataxia Patients and in a Mouse Model

Myriam Rai, Elisabetta Soragni, C. James Chou et al. · PLoS ONE · 2010 · 140 citations · Full text