Gian Luca Vita

Patterns of disease progression in type 2 and 3 SMA: Implications for clinical trials

Eugenio Mercuri, Richard S. Finkel, Jacqueline Montes et al. · Neuromuscular Disorders · 2015 · 215 citations · Full text

Life Sciences, Health Sciences, Medical Genetics +12

Histological effects of givinostat in boys with Duchenne muscular dystrophy

P. Bettica, Stefania Petrini, Valentina Doria et al. · Neuromuscular Disorders · 2016 · 207 citations · Full text

Medicine, Pediatrics, Pharmacotherapy +17

Long Term Natural History Data in Ambulant Boys with Duchenne Muscular Dystrophy: 36-Month Changes

Marika Pane, Elena Mazzone, Serena Sivo et al. · PLoS ONE · 2014 · 153 citations · Full text

Medicine, Rehabilitation Medicine, Mobility Rehabilitation +12

24 Month Longitudinal Data in Ambulant Boys with Duchenne Muscular Dystrophy

Elena Mazzone, Marika Pane, Maria Pia Sormani et al. · PLoS ONE · 2013 · 131 citations · Full text

Medicine, Pediatrics, Rehabilitation Medicine +14

A randomized placebo-controlled phase 3 trial of an antisense oligonucleotide, drisapersen, in Duchenne muscular dystrophy

Nathalie Goemans, Eugenio Mercuri, Hirofumi Komaki et al. · Neuromuscular Disorders · 2017 · 128 citations · Full text

Medicine, Molecular Medicine, Neuromuscular Disorders +7