Publication | Open Access
A randomized placebo-controlled phase 3 trial of an antisense oligonucleotide, drisapersen, in Duchenne muscular dystrophy
119
Citations
54
References
2017
Year
Duchenne Muscular DystrophyMedicineClinical TrialsDegenerative DiseaseAntisense OligonucleotideAntisense TherapyPharmacologyNeuromusculoskeletal Disorder
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