Antisense oligonucleotides enhance SLC20A2 expression and suppress brain calcification in a humanized mouse model

Miao Zhao, Xuewen Cheng, Lei Chen, Yi‐Heng Zeng, Kai-Jun Lin, Yun‐Lu Li, Ze-Hong Zheng, Huang Xue-jing, Dandan Zuo, Jun Guo,

Neuron · 2024 · 23 citations · 46 references

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