Sleeping Beauty mRNA-LNP enables stable rAAV transgene expression in mouse and NHP hepatocytes and improves vector potency

Philip M. Zakas, Sharon C. Cunningham, Ann Doherty, Eva B. van Dijk, Raed Ibraheim, Stephanie Yu, Befikadu D Mekonnen, Elizabeth J. English, Gang Sun, Matthew S Benczkowski,

Molecular Therapy · 2024 · 21 citations · 52 references

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