Vosoritide therapy in children with achondroplasia aged 3−59 months: a multinational, randomised, double-blind, placebo-controlled, phase 2 trial

C-Type Natriuretic Peptide Analogue Therapy in Children with Achondroplasia

Ravi Savarirayan, Melita Irving, Carlos A. Bacino et al. · New England Journal of Medicine · 2019 · 219 citations · Full text

Medicine, Clinical Sciences, Pharmacotherapy +6

Evaluation of the Therapeutic Potential of a CNP Analog in a Fgfr3 Mouse Model Recapitulating Achondroplasia

Florence Lorget, Nabil Kaci, Jeff Peng et al. · The American Journal of Human Genetics · 2012 · 209 citations · Full text

Life Sciences, Cell Biology, Genetics +6

Apnea and sudden unexpected death in infants with achondroplasia

Richard M. Pauli, Charles I. Scott, E. Robert Wassman et al. · The Journal of Pediatrics · 1984 · 205 citations

Medicine, Clinical Sciences, Pediatrics +12

Once-daily, subcutaneous vosoritide therapy in children with achondroplasia: a randomised, double-blind, phase 3, placebo-controlled, multicentre trial

Ravi Savarirayan, Louise Tofts, Melita Irving et al. · The Lancet · 2020 · 198 citations

Medicine, Pediatrics, Pharmacotherapy +2

Growth of the foramen magnum in achondroplasia

Jacqueline T. Hecht, William A. Horton, Cheryl S. Reid et al. · American Journal of Medical Genetics · 1989 · 135 citations · Full text

Medicine, Orthopaedic Surgery, Orthopedic Surgery +12