Publication | Open Access
Synthetic mRNA rescues very long-chain acyl-CoA dehydrogenase deficiency in patient fibroblasts and a murine model
16
Citations
42
References
2022
Year
FibrosisGeneticsMurine ModelSynthetic Mrna RescuesBiochemical GeneticsPatient FibroblastsGene ExpressionMedicineCell BiologyAlcohol DehydrogenasesCarbonyl Metabolism
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