Publication | Open Access
Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2): secondary analyses from an open-label trial
96
Citations
24
References
2022
Year
Type 1Firefish Part 2RehabilitationNeurologySpinal Muscular AtrophyMedicineSpinal DisorderOrthopaedic SurgeryNeuromusculoskeletal Disorder
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