Sebelipase alfa enzyme replacement therapy in Wolman disease: a nationwide cohort with up to ten years of follow-up - Concepedia

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Sebelipase alfa enzyme replacement therapy in Wolman disease: a nationwide cohort with up to ten years of follow-up

DOI Full Paper Access

27

Citations

18

References

2021

Year

Tanguy Demaret, Florence Lacaille, Camille Wicker, Jean‐Baptiste Arnoux, Juliette Bouchereau, Claire Belloche, Cyril Gitiaux, D. Grévent, Christine Broissand, Dalila Adjaoud,

Orphanet Journal of Rare Diseases

Nationwide CohortEnzyme Replacement TherapyClinical EpidemiologyPathologyWolman DiseaseMedicine

References

	Year	Citations

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