Concepedia
PubMed · 1973 · 29 citations · 1 references
MedicinePharmacologyClinical PharmacologyPharmacodynamicsAdverse Drug Reaction DetectionCardiovascular PharmacodynamicsDrug AllergyDrug Safety MonitoringBha ToxicitySafety And TolerabilityTreatment IntoleranceVascular Injury Response
1
Orphan drug development in muscular dystrophy: update on two large clinical trials of dystrophin rescue therapies.
Eric P. Hoffman, Edward M. Connor · PubMed · 2013 · 57 citations
Medicine, Molecular Genetics, Pharmacology +15