European Journal of Paediatric Neurology · 2021 · 25 citations · 23 references
Neurobiology Of DiseaseGaucher DiseaseType 3PediatricsEarly InitiationNeurologyNeuropathologyMedicine
23
Randomized, controlled trial of miglustat in Gaucher's disease type 3
Raphael Schiffmann, Edmond J. FitzGibbon, Chris Harris et al. · Annals of Neurology · 2008 · 232 citations · Full text