Publication | Closed Access

Addition of iptacopan, an oral factor B inhibitor, to eculizumab in patients with paroxysmal nocturnal haemoglobinuria and active haemolysis: an open-label, single-arm, phase 2, proof-of-concept trial

ThrombosisHematologyPharmacologyActive HaemolysisHemostasisPharmacotherapyPhase 2MedicineAnticoagulantParoxysmal Nocturnal Haemoglobinuria