Ophthalmology · 2021 · 164 citations · 27 references
MedicineNeurologyOphthalmologyGene TherapyNeuro-ophthalmologyOcular DiseaseEye DiseaseOcular Gene DeliveryOcular Gene TherapyOptic NeuropathiesVisual ImpairmentVisual Loss EvaluationHereditary Eye DiseaseHereditary Ocular DiseaseInherited Optic NeuropathiesLeber Hereditary Optic NeuropathyMitochondrial Dna MutationsVision Loss AssessmentVisual Field PerimetryVisual Function Loss
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Stephen R. Russell, Jean Bennett, Jennifer Wellman et al. · The Lancet · 2017 · 1.9K citations
A randomized placebo-controlled trial of idebenone in Leber’s hereditary optic neuropathy
Thomas Klopstock, Patrick Yu‐Wai‐Man, Konstantinos Dimitriadis et al. · Brain · 2011 · 569 citations · Full text
Medicine, Neurology, Ophthalmology +17