Efficacy and Safety of Intravitreal Gene Therapy for Leber Hereditary Optic Neuropathy Treated within 6 Months of Disease Onset

Nancy J. Newman, Patrick Yu‐Wai‐Man, Valério Carelli, Mark L. Moster, Valérie Biousse, Catherine Vignal, Robert C. Sergott, Thomas Klopstock, Alfredo A. Sadun, Piero Barboni,

Ophthalmology · 2021 · 164 citations · 27 references

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