Concepedia

Treating Bietti crystalline dystrophy in a high-fat diet-exacerbated murine model using gene therapy

Bin Qu, Shijing Wu, Guanyi Jiao, Xuan Zou, Zhikun Li, Lu Guo, Xuehan Sun, Cheng Huang, Zixi Sun, Ying Zhang,

Gene Therapy · 2020 · 28 citations · 33 references

DOI

Concepts

References

33

Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B

Amit C. Nathwani, Edward G. D. Tuddenham, Savita Rangarajan et al. · New England Journal of Medicine · 2011 · 1.8K citations · Full text

, , +13

Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B

Amit Nathwani, Ulreke M. Reiss, Edward G. D. Tuddenham et al. · New England Journal of Medicine · 2014 · 1.3K citations · Full text

, , +17

Gene therapy restores vision in a canine model of childhood blindness

Gregory M. Acland, Jharna Ray, Qí Zhāng et al. · Nature Genetics · 2001 · 1.2K citations

, , +16

Gene Therapy for Human Genetic Disease?

Theodore Friedmann, Richard O. Roblin · Science · 1972 · 797 citations

, , +8

Gene therapy clinical trials worldwide to 2017: An update

Samantha L. Ginn, Anais K. Amaya, Ian E. Alexander et al. · The Journal of Gene Medicine · 2018 · 778 citations

, , +15