RNAi-Based Gene Therapy Rescues Developmental and Epileptic Encephalopathy in a Genetic Mouse Model

Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis

David Adams, Alejandra González‐Duarte, William O’Riordan et al. · New England Journal of Medicine · 2018 · 2.9K citations · Full text

Life Sciences, Molecular Biology, Pharmacology +14

Analysis of AAV Serotypes 1–9 Mediated Gene Expression and Tropism in Mice After Systemic Injection

Carmela Zincarelli, Stephen Soltys, Giuseppe Rengo et al. · Molecular Therapy · 2008 · 1.5K citations · Full text

Life Sciences, Biology, Molecular Biology +15

Fluoro-Jade C results in ultra high resolution and contrast labeling of degenerating neurons

Larry Schmued, Chris C. Stowers, Andrew C. Scallet et al. · Brain Research · 2005 · 636 citations · Full text

Life Sciences, Neurobiology, Neuroscience +15

A Selective Activity-Dependent Requirement for Dynamin 1 in Synaptic Vesicle Endocytosis

Shawn M. Ferguson, Gabor Brasnjo, Mitsuko Hayashi et al. · Science · 2007 · 520 citations

Life Sciences, Cell Biology, Neuroscience +17

GTPase activity of dynamin and resulting conformation change are essential for endocytosis

Bruno Marks, Michael H. B. Stowell, Yvonne Vallis et al. · Nature · 2001 · 458 citations

Life Sciences, Cell Biology, Molecular Biology +14