Metformin treatment in young children with fragile X syndrome

Hazel Maridith Barlahan Biag, Laura A. Potter, Victoria Wilkins, Sumra Afzal, Alexis Rosvall, María Jimena Salcedo‐Arellano, Akash Rajaratnam, Ramiro Manzano-Núñez, Andrea Schneider, Flora Tassone,

Molecular Genetics & Genomic Medicine · 2019 · 65 citations · 40 references

DOIFull text

Open access

Abstract

These results support the need for a controlled trial of metformin in children with FXS under 7 years old whose brains are in a critical developmental window and thus may experience a greater degree of clinical benefit from metformin.

References

40