Molecular Therapy · 2019 · 53 citations · 50 references
Life SciencesBiotechnologyGeneticsCell TherapyGenome EditingRegenerative MedicineCrispr-based EngineeringCrispr-cas SystemsMuscle DifferentiationMuscular DystrophyStem Cell Gene TherapyTherapeutic Genome EditingAutologous Stem Cell TherapyCrispr-cas Genome EditingCrispr-cas9 Genome EditingCrispr-cas9 KnockoutGene CorrectionGene Editing For Cell TherapyInduced Pluripotent Stem Cell TherapySkeletal Muscle Wasting
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Induction of Pluripotent Stem Cells from Adult Human Fibroblasts by Defined Factors
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Easy quantitative assessment of genome editing by sequence trace decomposition
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A severe combined immunodeficiency mutation in the mouse
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Life Sciences, Genetics, Immunology +12