Gene Correction of LGMD2A Patient-Specific iPSCs for the Development of Targeted Autologous Cell Therapy

Sridhar Selvaraj, Neha R. Dhoke, James P. Kiley, Alba Judith Mateos-Aierdi, Sudheer Tungtur, Ricardo Mondragón-González, Grace Killeen, Vanessa K.P. Oliveira, Adolfo López de Munaín, Rita C. R. Perlingeiro

Molecular Therapy · 2019 · 53 citations · 50 references

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