Towards regulatory endorsement of drug development tools to promote the application of model-informed drug development in Duchenne muscular dystrophy

A study of cross-validation and bootstrap for accuracy estimation and model selection

Ron Kohavi · 1995 · 10.7K citations

Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management

K. Bushby, Richard S. Finkel, David J. Birnkrant et al. · The Lancet Neurology · 2009 · 2K citations

Part 1, Kinesiology, Psychiatry +9

Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy: a prospective cohort study

Craig M. McDonald, Erik Henricson, Richard T. Abresch et al. · The Lancet · 2017 · 446 citations

Long-term Effects, Duchenne Muscular Dystrophy, Degenerative Disease +4

Likelihood based approaches to handling data below the quantification limit using NONMEM VI

Jae Eun Ahn, Mats O. Karlsson, Adrian Dunne et al. · Journal of Pharmacokinetics and Pharmacodynamics · 2008 · 329 citations

Engineering, Data Science, Nonmem Vi +6

Improvement of survival in Duchenne Muscular Dystrophy: retrospective analysis of 835 patients.

Luigia Passamano, Antonella Taglia, Alberto Palladino et al. · PubMed · 2012 · 326 citations · Full text

Heart Failure, Pediatric Heart Disease, Retrospective Analysis +16