Intracerebral gene therapy in children with mucopolysaccharidosis type IIIB syndrome: an uncontrolled phase 1/2 clinical trial - Concepedia

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Intracerebral gene therapy in children with mucopolysaccharidosis type IIIB syndrome: an uncontrolled phase 1/2 clinical trial

226

Citations

26

References

2017

Year

Marc Tardieu, Michel Zérah, Marie‐Lise Gougeon, Jérôme Ausseil, Stéphanie de Bournonville, B. Husson, Dimitrios Zafeiriou, Giancarlo Parenti, Philippe Bourget, Béatrice Poirier,

The Lancet Neurology

Translational MedicineUncontrolled Phase 1/2Intracerebral Gene TherapyNeurologyMultiple SclerosisNeuropathologyMedicineLysosomal Storage Disease

References

	Year	Citations

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