Concepedia

Danazol Treatment for Telomere Diseases

Danielle M. Townsley, Bogdan Dumitriu, Delong Liu, Angélique Biancotto, Barbara Weinstein, Christina Chen, Nathan Hardy, Andrew D. Mihalek, Shilpa Lingala, Yun Ju Kim,

New England Journal of Medicine · 2016 · 391 citations · 34 references

DOIFull text

Open access

Abstract

In our study, treatment with danazol led to telomere elongation in patients with telomere diseases. (Funded by the National Institutes of Health; ClinicalTrials.gov number, NCT01441037.).

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