Expression of ΔF508 CFTR in normal mouse lung after site-specific modification of CFTR sequences by SFHR
Kk Goncz,
Alessia Colosimo,
Bruno Dallapiccola,
Lucie Gagné,
Keelung Hong,
Giuseppe Novelli,
Demetrios Papahadjopoulos,
Teiji Sawa,
Hans Schreier,
J. P. Wiener-Kronish,
Gene Therapy · 2001 · 77 citations · 23 references