Publication | Open Access
A Single CRISPR-Cas9 Deletion Strategy that Targets the Majority of DMD Patients Restores Dystrophin Function in hiPSC-Derived Muscle Cells
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Citations
22
References
2016
Year
Off-target EffectDegenerative DiseaseGenome EngineeringGene EditingGenome EditingSystems BiologyMedicineCell BiologyCrisprHipsc-derived Muscle Cells
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