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Longitudinal effect of eteplirsen versus historical control on ambulation in <scp>D</scp> uchenne muscular dystrophy

DOIFull Paper Access

495

Citations

42

References

2015

Year

Jerry R. Mendell, Nathalie Goemans, Linda Lowes, Lindsay N. Alfano, Katherine Berry, James Shao, Edward M. Kaye, Eugenio Mercuri
Annals of Neurology

Abstract

Over 3 years of follow-up, eteplirsen-treated patients showed a slower rate of decline in ambulation assessed by 6MWT compared to untreated matched HC.

References

YearCitations

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