Very Early Treatment for Infantile-Onset Pompe Disease Contributes to Better Outcomes

The Danger Model: A Renewed Sense of Self

Polly Matzinger · Science · 2002 · 4.2K citations

Life Sciences, Immunology, Adaptive Immunity +13

A Randomized Study of Alglucosidase Alfa in Late-Onset Pompe's Disease

Ans T. van der Ploeg, Paula R. Clemens, Deyanira Corzo et al. · New England Journal of Medicine · 2010 · 747 citations · Full text

Life Sciences, Internal Medicine, Pharmacotherapy +13

A retrospective, multinational, multicenter study on the natural history of infantile-onset Pompe disease

Priya S. Kishnani, Wuh‐Liang Hwu, Hanna Mandel et al. · The Journal of Pediatrics · 2006 · 585 citations

Medicine, Neurology, Pediatrics +3

Cross-reactive immunologic material status affects treatment outcomes in Pompe disease infants

Priya S. Kishnani, Paula Goldenberg, Stephanie DeArmey et al. · Molecular Genetics and Metabolism · 2009 · 379 citations

Medicine, Immunology, Pediatrics +5

Construction and validation of the Alberta Infant Motor Scale (AIMS).

Martha C. Piper, Lynn Pinnell, Thomas O. Maguire et al. · PubMed · 1993 · 353 citations

Education, Human Development, Pediatrics +16