Human Gene Therapy · 1999 · 48 citations · 22 references
Life SciencesGeneticsMolecular BiologyGene DeliveryGene TherapyRecombinant Dna TechnologyAmino Acid Metabolism DisordersEnzyme DeficienciesGenetic DisordersSafety Of Gene TherapyViral Vector-mediated TransgenesisAdenoviral TransgenesisAdenoviral VectorsAdenovirus BiologyAdenovirus VectorsOrnithine Transcarbamylase Deficiency
protocol for clinical trial involving Jesse Gelsinger
22
Neurologic Outcome in Children with Inborn Errors of Urea Synthesis
Michael E. Msall, Mark L. Batshaw, Richard A. Suss et al. · New England Journal of Medicine · 1984 · 412 citations
Medicine, Neurology, Pediatrics +16