Publication | Closed Access

Oligonucleotides against a splicing enhancer sequence led to dystrophin production in muscle cells from a Duchenne muscular dystrophy patient

Muscle CellsSkeletal MuscleNatural SciencesGeneticsOligonucleotideMolecular BiologyDegenerative DiseaseSplicing Enhancer SequenceAntisense TherapyGene ExpressionMedicineCell BiologySplicing Variant