Targeting nuclear RNA for in vivo correction of myotonic dystrophy

Thurman M. Wheeler, Andrew J. Leger, Sanjay K. Pandey, A. Robert MacLeod, Masayuki Nakamori, Seng H. Cheng, Bruce M. Wentworth, C. Frank Bennett, Charles A. Thornton

Nature · 2012 · 491 citations · 38 references

DOIFull text

Open access

Concepts

References

38