Nature · 2012 · 491 citations · 38 references
Life SciencesGeneticsMolecular BiologyGene DeliveryGene TherapyGenome EditingIn Vivo Gene TherapyMessenger Rna DeliveryMuscular DystrophyRna EditingRna InterferenceDystrophin DeficiencyEditing For Muscular DystrophyMuscular Dystrophy PathophysiologyNuclear Rna EditingRna Editing In DiseaseRna-based Gene Therapy
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