Publication | Open Access
Functional Correction of Large Factor VIII Gene Chromosomal Inversions in Hemophilia A Patient-Derived iPSCs Using CRISPR-Cas9
299
Citations
36
References
2015
Year
Functional CorrectionGene TherapiesGeneticsGenetic EngineeringPathologyMolecular GeneticsGene EditingGenome EditingGenome EngineeringOff-target EffectMedicineCrispr
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