Publication | Closed Access
Genetic conversion of an SMN2 gene to SMN1: A novel approach to the treatment of spinal muscular atrophy
33
Citations
30
References
2007
Year
Genetic ConversionGene TherapiesRare DiseasesGenetic DisorderGeneticsMolecular BiologyGenetic EngineeringDegenerative DiseaseSpinal Muscular AtrophyDisease Gene IdentificationMedicineSmn2 Gene
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