Concepedia

Targeted conversion of the transthyretin gene in vitro and in vivo

Masaaki Nakamura, Yukio Ando, Shunji Nagahara, Akihiko Sano, Takahiro Ochiya, Shuichiro Maeda, Takahiro Kawaji, Mamoru Ogawa, Akira Hirata, Hisayasu Terazaki,

Gene Therapy · 2004 · 55 citations · 32 references

DOI

Concepts

References

32

Clinical improvement and amyloid regression after liver transplantation in hereditary transthyretin amyloidosis

Gösta Holmgren, Lars Steen, Ole B. Suhr et al. · The Lancet · 1993 · 581 citations

, , +17

Sequence requirements of the hammerhead RNA self-cleavage reaction

Duane E. Ruffner, Gary D. Stormo, Olke C. Uhlenbeck · Biochemistry · 1990 · 471 citations

, , +11

Correction of the Mutation Responsible for Sickle Cell Anemia by an RNA-DNA Oligonucleotide

Allyson Cole-Strauss, Kyonggeun Yoon, Yufei Xiang et al. · Science · 1996 · 319 citations

, , +17

In vivo site-directed mutagenesis of the factor IX gene by chimeric RNA/DNA oligonucleotides

B.T. Kren, Paramita Bandyopadhyay, Clifford J. Steer · Nature Medicine · 1998 · 259 citations

, , +11

New delivery system for plasmid DNA in vivo using atelocollagen as a carrier material: the Minipellet

Takahiro Ochiya, Yasushi Takahama, Shunji Nagahara et al. · Nature Medicine · 1999 · 235 citations

, , +16