Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease - Concepedia

Concepedia

Publication | Open Access

Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease

DOI Full Paper Access

290

Citations

18

References

2009

Year

Marc Nicolino, Barry J. Byrne, J. Edmund Wraith, Nancy Leslie, Hanna Mandel, David R. Freyer, Georgianne L. Arnold, Enikö K. Pivnick, C. J. Ottinger, Peter N. Robinson,

Genetics in Medicine

Pediatric EpidemiologyClinical EpidemiologyPediatricsAdvanced Pompe DiseaseClinical OutcomesSubstrate Reduction TherapyAlglucosidase AlfaPublic HealthMedicinePaediatric Medicine

References

	Year	Citations

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