Léon P. F. Winkel

Long-Term Intravenous Treatment of Pompe Disease With Recombinant Human α-Glucosidase From Milk

Johanna M. P. van den Hout, Joep H. J. Kamphoven, Léon P. F. Winkel et al. · PEDIATRICS · 2004 · 354 citations

Life Sciences, Biochemistry, Molecular Medicine +12

Enzyme replacement therapy in late‐onset Pompe's disease: A three‐year follow‐up

Léon P. F. Winkel, Johanna M. P. van den Hout, Joep H. J. Kamphoven et al. · Annals of Neurology · 2004 · 231 citations

Life Sciences, Biochemistry, Enzymology +12

Disease severity in children and adults with Pompe disease related to age and disease duration

M.L.C. Hagemans, Léon P. F. Winkel, Wim C.J. Hop et al. · Neurology · 2005 · 185 citations

Public Health, Child Health, Pediatrics +11

Late-onset Pompe disease primarily affects quality of life in physical health domains

M.L.C. Hagemans, A. Cecile J.W. Janssens, Léon P. F. Winkel et al. · Neurology · 2004 · 115 citations

Pharmacy, Health Sciences, Internal Medicine +17

Morphological changes in muscle tissue of patients with infantile Pompe's disease receiving enzyme replacement therapy

Léon P. F. Winkel, Joep H. J. Kamphoven, Hannerieke J.M.P. van den Hout et al. · Muscle & Nerve · 2003 · 103 citations

Medicine, Pathology, Pediatrics +17