Journal of Controlled Release · 2013 · 163 citations · 28 references
PharmacyOphthalmologyPharmaceuticsDrug DeliveryGene DeliveryNanoparticle Drug DeliveryOcular Gene DeliveryOcular Gene TherapyOcular NanocarriersOcular Targeted DeliveryRetinal NeurobiologyRetinal Pigment EpitheliumDrug Delivery To The RetinaGene Delivery NanocarriersGene Delivery NanoparticlesNiosome Drug DeliveryTargeted Delivery To The Retina
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Safety and Efficacy of Gene Transfer for Leber's Congenital Amaurosis
Albert M. Maguire, Francesca Simonelli, Eric A. Pierce et al. · New England Journal of Medicine · 2008 · 2.1K citations · Full text
Medicine, Genetics, Ophthalmology +17
Effect of Gene Therapy on Visual Function in Leber's Congenital Amaurosis
James Bainbridge, Alexander J. Smith, Susie S. Barker et al. · New England Journal of Medicine · 2008 · 1.9K citations · Full text
Medicine, Genetics, Ophthalmology +15