Concepedia

Biochemical and pharmacological characterization of different recombinant acid α-glucosidase preparations evaluated for the treatment of Pompe disease

Alison McVie‐Wylie, K.L. Lee, Hengheng Qiu, Xin Jin, Russell Gotschall, Beth L. Thurberg, Chris Rogers, Nina Raben, M. W. O'CALLAGHAN, William M. Canfield,

Molecular Genetics and Metabolism · 2008 · 96 citations · 28 references

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References

28

Cleavage of Structural Proteins during the Assembly of the Head of Bacteriophage T4

Ulrich K. Laemmli · Nature · 1970 · 251.6K citations

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Recombinant human acid α-glucosidase

Priya S. Kishnani, Deya Corzo, Marc Nicolino et al. · Neurology · 2006 · 772 citations · Full text

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Long-Term Intravenous Treatment of Pompe Disease With Recombinant Human α-Glucosidase From Milk

Johanna M. P. van den Hout, Joep H. J. Kamphoven, Léon P. F. Winkel et al. · PEDIATRICS · 2004 · 354 citations

, , +12

Recombinant human acid α-glucosidase enzyme therapy for infantile glycogen storage disease type II: Results of a phase I/II clinical trial

Andrea Amalfitano, A. Resai Bengur, Richard P. Morse et al. · Genetics in Medicine · 2001 · 347 citations · Full text

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Targeted Disruption of the Acid α-Glucosidase Gene in Mice Causes an Illness with Critical Features of Both Infantile and Adult Human Glycogen Storage Disease Type II

Nina Raben, Kanneboyina Nagaraju, Eunice Lee et al. · Journal of Biological Chemistry · 1998 · 297 citations · Full text

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