Neuromuscular Disorders · 1997 · 77 citations · 15 references
MedicineGeneticsMolecular MedicineGene TherapyMedical GeneticsTransgenic Animal ModelsAnimal ModelExperimental Disease ModelsGenetic DisordersIn Vivo Gene TherapyMuscular DystrophySafety Of Gene TherapyDystrophin DeficiencyGene Therapy In Animal ModelsMuscle Gene TherapyMuscle Regeneration Gene TherapyMuscular Dystrophy GeneticsMuscular Dystrophy PathophysiologyTherapeutic Trials
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Dystrophin: The protein product of the duchenne muscular dystrophy locus
Eric P. Hoffman, Robert H. Brown, Louis M. Kunkel · Cell · 1987 · 4.7K citations
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Human dystrophin expression in mdx mice after intramuscular injection of DNA constructs
Gyula Acsádi, George Dickson, Donald R. Love et al. · Nature · 1991 · 486 citations
The homologue of the Duchenne locus is defective in X-linked muscular dystrophy of dogs
Barry J. Cooper, Nena J. Winand, Hansell H. Stedman et al. · Nature · 1988 · 429 citations