Retinoschisin gene therapy in photoreceptors, Müller glia or all retinal cells in the Rs1h−/− mouse

In Vivo–Directed Evolution of a New Adeno-Associated Virus for Therapeutic Outer Retinal Gene Delivery from the Vitreous

Deniz Dalkara, Leah C. Byrne, R. R. Klimczak et al. · Science Translational Medicine · 2013 · 733 citations

Pharmacy, Biotechnology, Ophthalmology +16

Production and characterization of adeno-associated viral vectors

Joshua C. Grieger, Vivian W. Choi, R. Jude Samulski · Nature Protocols · 2006 · 598 citations

Life Sciences, Biotechnology, Molecular Biology +12

Positional cloning of the gene associated with X-linked juvenile retinoschisis

Christian Sauer, Andrea Gehrig, Regina Warneke-Wittstock et al. · Nature Genetics · 1997 · 497 citations

Medicine, Genetics, Molecular Genetics +12

Universal Real-Time PCR for the Detection and Quantification of Adeno-Associated Virus Serotype 2-Derived Inverted Terminal Repeat Sequences

Christine Aurnhammer, Maren Haase, Nadine Muether et al. · Human Gene Therapy Methods · 2012 · 490 citations

Life Sciences, Biotechnology, Molecular Biology +14

Inactivation of the murine X-linked juvenile retinoschisis gene, Rs1h, suggests a role of retinoschisin in retinal cell layer organisation and synaptic structure

Heinrich Schrewe, Andrea Gehrig, Christoph Friedburg et al. · University of Birmingham Research Portal (University of Birmingham) · 2002 · 213 citations

Medicine, Genetics, Molecular Genetics +17