Hepatocytes corrected by gene therapy are selected in vivo in a murine model of hereditary tyrosinaemia type I

Ken Overturf, Muhsen Al-Dhalimy, Robert M. Tanguay, Mark Brantly, Ching-Nan Ou, Milton J. Finegold, Markus Grompe

Nature Genetics · 1996 · 555 citations · 52 references

Concepts

References

52